#gene-therapy

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#vision-loss
Wearables
fromNature
1 month ago

The search for solutions to geographic atrophy of the retina

Age-related macular degeneration (AMD) leads to progressive vision loss, significantly impacting independence, but recent drug approvals offer hope for treatment.
OMG science
fromIrish Independent
7 months ago

Trinity College Dublin scientists make breakthrough on gene therapy for eye disease described as 'silent thief of sight'

Gene therapy shows promise in protecting vision by improving retinal cell function in glaucoma patients.
fromCbsnews
16 hours ago
OMG science

New research shows promise for restoring vision for people with glaucoma, other conditions

New research reveals potential therapies for retinal damage using gene therapy to combat Prox-1 protein's inhibitory effect on retinal regeneration.
fromNature
11 months ago
Medicine

CRISPR therapy restores some vision to people with blindness

CRISPR-based gene therapy improved vision in individuals with inherited blindness.
Wearables
fromNature
1 month ago

The search for solutions to geographic atrophy of the retina

Age-related macular degeneration (AMD) leads to progressive vision loss, significantly impacting independence, but recent drug approvals offer hope for treatment.
OMG science
fromIrish Independent
7 months ago

Trinity College Dublin scientists make breakthrough on gene therapy for eye disease described as 'silent thief of sight'

Gene therapy shows promise in protecting vision by improving retinal cell function in glaucoma patients.
fromCbsnews
16 hours ago
OMG science

New research shows promise for restoring vision for people with glaucoma, other conditions

New research reveals potential therapies for retinal damage using gene therapy to combat Prox-1 protein's inhibitory effect on retinal regeneration.
fromNature
11 months ago
Medicine

CRISPR therapy restores some vision to people with blindness

CRISPR-based gene therapy improved vision in individuals with inherited blindness.
more#vision-loss
#health-innovation
Growth hacking
fromwww.dailymail.co.uk
1 month ago

Inside the secret island where wealthy people go to alter their DNA

Roatan is attracting ultra-wealthy individuals seeking experimental gene therapies due to its lack of regulations around such treatments.
Growth hacking
fromEntrepreneur
1 day ago

This Gene Therapy Startup Wants to Change the Way We Age | Entrepreneur

Minicircle aims to slow aging and enhance biological function through a quick gene therapy injection.
Growth hacking
fromwww.dailymail.co.uk
1 month ago

Inside the secret island where wealthy people go to alter their DNA

Roatan is attracting ultra-wealthy individuals seeking experimental gene therapies due to its lack of regulations around such treatments.
Growth hacking
fromEntrepreneur
1 day ago

This Gene Therapy Startup Wants to Change the Way We Age | Entrepreneur

Minicircle aims to slow aging and enhance biological function through a quick gene therapy injection.
more#health-innovation
#patient-experience
OMG science
fromwww.npr.org
7 months ago

Sickle cell gene therapies roll out slowly

FDA has approved the first genetic treatments for sickle cell disease, offering new hope to patients like Olaide Adekanbi.
OMG science
fromHarvard Gazette
1 week ago

Gene therapy frees hemophilia patient from constant worry, needles - Harvard Gazette

Gene therapy is providing hope and improved quality of life for hemophilia patients.
fromwww.nytimes.com
11 months ago
Medicine

First Patient Begins Newly Approved Sickle Cell Gene Therapy

Commercially approved gene therapy offers hope to sickle cell patients like Kendric Cromer, potentially leading to a cure.
OMG science
fromwww.npr.org
7 months ago

Sickle cell gene therapies roll out slowly

FDA has approved the first genetic treatments for sickle cell disease, offering new hope to patients like Olaide Adekanbi.
OMG science
fromHarvard Gazette
1 week ago

Gene therapy frees hemophilia patient from constant worry, needles - Harvard Gazette

Gene therapy is providing hope and improved quality of life for hemophilia patients.
fromwww.nytimes.com
11 months ago
Medicine

First Patient Begins Newly Approved Sickle Cell Gene Therapy

Commercially approved gene therapy offers hope to sickle cell patients like Kendric Cromer, potentially leading to a cure.
more#patient-experience
#duchenne-muscular-dystrophy
SF parents
fromCbsnews
1 month ago

Northern Minnesota boy is first American to receive groundbreaking treatment for muscular dystrophy

Colton Belluzzo received groundbreaking gene therapy for Duchenne muscular dystrophy, showing promise in slowing disease progression.
EU data protection
fromwww.mcall.com
1 month ago

Patient dies following muscular dystrophy gene therapy, Sarepta reports

A patient died from acute liver injury while using Sarepta's Elevidys gene therapy for muscular dystrophy, causing a major stock market reaction.
fromCbsnews
2 months ago
Miscellaneous

Minneapolis parents share journey of having two sons with rare muscle-wasting disorder

The Kasner family faces Duchenne muscular dystrophy with resilience and a strong support network, embracing love and life despite the challenges.
SF parents
fromCbsnews
1 month ago

Northern Minnesota boy is first American to receive groundbreaking treatment for muscular dystrophy

Colton Belluzzo received groundbreaking gene therapy for Duchenne muscular dystrophy, showing promise in slowing disease progression.
EU data protection
fromwww.mcall.com
1 month ago

Patient dies following muscular dystrophy gene therapy, Sarepta reports

A patient died from acute liver injury while using Sarepta's Elevidys gene therapy for muscular dystrophy, causing a major stock market reaction.
fromCbsnews
2 months ago
Miscellaneous

Minneapolis parents share journey of having two sons with rare muscle-wasting disorder

The Kasner family faces Duchenne muscular dystrophy with resilience and a strong support network, embracing love and life despite the challenges.
more#duchenne-muscular-dystrophy
OMG science
fromNews Center
1 month ago

Uncovering New Therapeutic Targets for Pediatric Epilepsy - News Center

Researchers have identified new mechanisms in Dravet syndrome that highlight novel therapeutic targets, particularly in intronic regions of the SCN1A gene.
#medical-innovation
Parenting
fromwww.bbc.com
2 months ago

Gene therapy experiment gives children 'life-changing' sight boost

Gene therapy has significantly improved the vision of toddlers born with severe childhood blindness, providing life-changing outcomes.
Medicine
fromwww.nytimes.com
1 month ago

Mutated DNA Restored to Normal in Gene Therapy Advance

A single infusion successfully corrected a mutated gene, marking a significant advancement in gene therapy.
This precision targeting could revolutionize treatment for various genetic diseases.
fromenglish.elpais.com
3 months ago
OMG science

From brain maps to living bridges: The innovations set to reshape life in 2025

2025 is poised to be a transformative year for neuroscience with breakthroughs in brain mapping and AI-led therapies.
fromwww.theguardian.com
8 months ago
Medicine

NHS to offer life-changing' gene therapy for blood disorder thalassaemia

Casgevy gene therapy approved for severe thalassaemia on NHS in England, potentially offering a lifetime cure with significant benefits for patients.
Parenting
fromwww.bbc.com
2 months ago

Gene therapy experiment gives children 'life-changing' sight boost

Gene therapy has significantly improved the vision of toddlers born with severe childhood blindness, providing life-changing outcomes.
Medicine
fromwww.nytimes.com
1 month ago

Mutated DNA Restored to Normal in Gene Therapy Advance

A single infusion successfully corrected a mutated gene, marking a significant advancement in gene therapy.
This precision targeting could revolutionize treatment for various genetic diseases.
OMG science
fromenglish.elpais.com
3 months ago

From brain maps to living bridges: The innovations set to reshape life in 2025

2025 is poised to be a transformative year for neuroscience with breakthroughs in brain mapping and AI-led therapies.
fromwww.theguardian.com
8 months ago
Medicine

NHS to offer life-changing' gene therapy for blood disorder thalassaemia

Casgevy gene therapy approved for severe thalassaemia on NHS in England, potentially offering a lifetime cure with significant benefits for patients.
more#medical-innovation
Mental health
fromNature
1 month ago

Why women's brains are more resilient: it could be their 'silent' X chromosome

The second X chromosome in females may guard against cognitive decline and aging.
#vision-restoration
Parenting
fromwww.standard.co.uk
2 months ago

Gene therapy experiment gives children 'life-changing' sight boost at London hospital

Pioneering gene therapy restores sight in young children with a rare genetic condition.
fromwww.dw.com
11 months ago
OMG science

Gene therapy trials treat inherited blindness and deafness DW 05/09/2024

The article highlights the groundbreaking achievement of restoring hearing and vision through gene therapy in children with rare genetic mutations.
Parenting
fromwww.standard.co.uk
2 months ago

Gene therapy experiment gives children 'life-changing' sight boost at London hospital

Pioneering gene therapy restores sight in young children with a rare genetic condition.
OMG science
fromwww.dw.com
11 months ago

Gene therapy trials treat inherited blindness and deafness DW 05/09/2024

The article highlights the groundbreaking achievement of restoring hearing and vision through gene therapy in children with rare genetic mutations.
more#vision-restoration
#medical-research
fromCancer
2 months ago
OMG science

Promising treatment for recurrent respiratory papillomatosis

PRGN-2012 shows promise as a gene therapy for recurrent respiratory papillomatosis, potentially reducing the need for multiple surgeries.
fromCancer
2 months ago
OMG science

Promising treatment for recurrent respiratory papillomatosis

PRGN-2012 shows promise as a gene therapy for recurrent respiratory papillomatosis, potentially reducing the need for multiple surgeries.
more#medical-research
#biotechnology
fromSilicon Canals
6 months ago
European startups

In other news this week: Knave secures 225M, London-based Purespring raises 95M, VERBUND X Ventures invests in Ausrtia's Easelink, and more - Silicon Canals

Tech innovations in October highlighted significant funding rounds for companies like Knave, Purespring, and Basecamp Research.
fromSilicon Canals
3 months ago
Medicine

Amsterdam-based biotech company uniQure sets this share price for 73M public offering: Know more - Silicon Canals

uniQure plans to raise $75M through a public offering amid promising progress in gene therapies for Huntington's disease.
fromSilicon Canals
6 months ago
European startups

In other news this week: Knave secures 225M, London-based Purespring raises 95M, VERBUND X Ventures invests in Ausrtia's Easelink, and more - Silicon Canals

Tech innovations in October highlighted significant funding rounds for companies like Knave, Purespring, and Basecamp Research.
fromSilicon Canals
3 months ago
Medicine

Amsterdam-based biotech company uniQure sets this share price for 73M public offering: Know more - Silicon Canals

uniQure plans to raise $75M through a public offering amid promising progress in gene therapies for Huntington's disease.
more#biotechnology
#crispr
OMG science
fromThe Atlantic
4 months ago

The Most Important Breakthroughs of 2024

2023 highlights include breakthroughs in gene therapy for sickle-cell anemia and a new HIV prevention drug that shows remarkable efficacy.
OMG science
fromWIRED
3 months ago

Correcting Genetic Spelling Errors With Next-Generation Crispr

Sam Berns' life epitomizes the urgent need for advancements in genetic treatments, particularly for disorders like progeria that code for rapid aging.
OMG science
fromThe Atlantic
4 months ago

The Most Important Breakthroughs of 2024

2023 highlights include breakthroughs in gene therapy for sickle-cell anemia and a new HIV prevention drug that shows remarkable efficacy.
OMG science
fromWIRED
3 months ago

Correcting Genetic Spelling Errors With Next-Generation Crispr

Sam Berns' life epitomizes the urgent need for advancements in genetic treatments, particularly for disorders like progeria that code for rapid aging.
more#crispr
Medicine
fromenglish.elpais.com
4 months ago

Strimvelis, the gene therapy rejected by the pharmaceutical industry that has saved Aitana

Gene therapy saved Aitana's life after she was diagnosed with a severe immune deficiency.
The Strimvelis treatment faced discontinuation, emphasizing the challenge of sustaining innovative medical therapies.
OMG science
fromMail Online
5 months ago

Scientists grow human brains in space to treat Alzheimer's

Microgravity facilitates rapid growth of brain organoids, enabling critical research into treatments for Alzheimer's, Parkinson's, and spinal injuries.
Medicine
fromwww.mercurynews.com
7 months ago

Cures for rare diseases now exist. Employers don't want to pay

The rise of multimillion-dollar gene therapies is pushing employers to drop coverage, leaving families in desperate situations.
Growth hacking
from24/7 Wall St.
7 months ago

Goldman Sachs Recommends These 3 Growth Stocks As Strong Buys in September

Goldman Sachs identifies three compelling growth stocks worth considering, signaling a shift towards diverse sectors amidst a technology market rotation.
Medicine
fromWIRED
8 months ago

How Do You Get Drugs to the Brain? Maybe Try a Parasite

Toxoplasma engineered to deliver proteins may offer treatment for brain disorders like Rett syndrome and neurodegenerative diseases.
fromwww.mercurynews.com
11 months ago
OMG science

Breakthrough therapies at Stanford are saving lives. Can we afford them?

Cell and gene therapies offer promising medical solutions but come with a hefty price tag, raising concerns about availability and affordability.
#medical-breakthrough
more#medical-breakthrough
fromtime.com
11 months ago
OMG science

Stuart Orkin

Dr. Stuart Orkin's research on identifying genes regulating fetal hemoglobin led to a revolutionary gene therapy for sickle cell disease using CRISPR technology.
OMG science
fromNature
10 months ago

Daily briefing: 'Open-washing' plagues big AI

Open-source AI not as transparent as claimed
Low-frequency vibrations trigger mouse sexual behaviors
Importance of research putting individuals at the heart of schizophrenia study
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